A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease

Phase 1/2 study testing SPK-10001 in Huntington's disease.

RecruitingPhase 1 / Phase 2GeneticClinicalTrials.govTreatment trial
Recruiting in: Boston, Cincinnati, Columbus +2 more, United States
Preparing a short plain-English summary.

Fenix helps people discover research. It does not provide medical advice or determine eligibility.